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Diffuse cutaneous systemic sclerosis

ORPHA:220393Clinical subtypeMultigenic/multifactorial, Not applicableAdult

Ассоциированные гены (5)

CAV1
caveolin 1
Major susceptibility factor in
OMIM: 601047
HLA-DRB1
major histocompatibility complex, class II, DR beta 1
Major susceptibility factor in
OMIM: 142857
CCN2
cellular communication network factor 2
Major susceptibility factor in
OMIM: 121009
IRF5
interferon regulatory factor 5
Major susceptibility factor in
OMIM: 607218
CCR6
C-C motif chemokine receptor 6
Major susceptibility factor in
OMIM: 601835

Фенотипы (26)

Очень частый (80–99%)7
HP:0000951Abnormality of the skin
HP:0002020Gastroesophageal reflux
HP:0002094Dyspnea
HP:0002113Pulmonary infiltrates
HP:0002960Autoimmunity
HP:0100520Oliguria
HP:0100958Narrow foramen obturatorium
Частый (30–79%)13
HP:0000217Xerostomia
HP:0000670Carious teeth
HP:0001324Muscle weakness
HP:0001369Arthritis
HP:0001371Flexion contracture
HP:0002015Dysphagia
HP:0002024Malabsorption
HP:0002206Pulmonary fibrosis
HP:0002797Osteolysis
HP:0002829Arthralgia
HP:0030016Dyspareunia
HP:0100585Telangiectasia of the skin
HP:0200042Skin ulcer
Периодический (5–29%)6
HP:0000083Renal insufficiency
HP:0001635Congestive heart failure
HP:0002017Nausea and vomiting
HP:0002092Pulmonary arterial hypertension
HP:0030142Abnormal bowel sounds
HP:0100735Hypertensive crisis

Эпидемиология (2)

Point prevalence
1-9 / 100 000
Taiwan, Province of China
Annual incidence
1-9 / 100 000
Taiwan, Province of China

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы