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Progeroid syndrome, Petty type

ORPHA:2963Clinical subtypeAutosomal dominantNeonatal

Ассоциированные гены (1)

SLC25A24
solute carrier family 25 member 24
Disease-causing germline mutation(s) in
OMIM: 608744

Фенотипы (28)

Очень частый (80–99%)28
HP:0000232Everted lower lip vermilion
HP:0000260Wide anterior fontanel
HP:0000286Epicanthus
HP:0000303Mandibular prognathia
HP:0000337Broad forehead
HP:0000486Strabismus
HP:0000574Thick eyebrow
HP:0000973Cutis laxa
HP:0001508Failure to thrive
HP:0001511Intrauterine growth retardation
HP:0001537Umbilical hernia
HP:0001582Redundant skin
HP:0001595Abnormality of the hair
HP:0001597Abnormality of the nail
HP:0002230Generalized hirsutism
HP:0002299Brittle hair
HP:0003758Reduced subcutaneous adipose tissue
HP:0004322Short stature
HP:0004331Decreased skull ossification
HP:0007477Abnormal dermatoglyphics
HP:0007495Prematurely aged appearance
HP:0007740Long eyelashes in irregular rows
HP:0008070Sparse hair
HP:0009721Shagreen patch
HP:0009804Tooth agenesis
HP:0009882Short distal phalanx of finger
HP:0100578Lipoatrophy
HP:0000358Posteriorly rotated ears

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы