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Self-limited infantile epilepsy

ORPHA:306DiseaseAutosomal dominantInfancy, Neonatal

Ассоциированные гены (5)

SCN8A
sodium voltage-gated channel alpha subunit 8
Disease-causing germline mutation(s) (gain of function) in
OMIM: 600702
SCN2A
sodium voltage-gated channel alpha subunit 2
Disease-causing germline mutation(s) in
OMIM: 182390
KCNQ2
potassium voltage-gated channel subfamily Q member 2
Disease-causing germline mutation(s) in
OMIM: 602235
KCNQ3
potassium voltage-gated channel subfamily Q member 3
Disease-causing germline mutation(s) in
OMIM: 602232
PRRT2
proline rich transmembrane protein 2
Disease-causing germline mutation(s) in
OMIM: 614386

Фенотипы (34)

Очень частый (80–99%)2
HP:0002372Normal interictal EEG
HP:0032807Neonatal seizure
Частый (30–79%)17
HP:0001250Seizure
HP:0001266Choreoathetosis
HP:0001332Dystonia
HP:0002072Chorea
HP:0002104Apnea
HP:0002266Focal clonic seizure
HP:0002305Athetosis
HP:0002384Focal impaired awareness seizure
HP:0004305Involuntary movements
HP:0007166Paroxysmal dyskinesia
HP:0007334Bilateral tonic-clonic seizure with focal onset
HP:0007359Focal-onset seizure
HP:0010818Generalized tonic seizure
HP:0011153Focal motor seizure
HP:0011167Focal tonic seizure
HP:0011169Generalized clonic seizure
HP:0032755Focal impaired awareness autonomic seizure
Периодический (5–29%)10
HP:0000961Cyanosis
HP:0001276Hypertonia
HP:0002069Bilateral tonic-clonic seizure
HP:0002121Generalized non-motor (absence) seizure
HP:0011172Complex febrile seizure
HP:0012002Experiential epileptic aura
HP:0032678Eyelid myoclonia seizure
HP:0032823Neonatal electro-clinical seizure with behavior arrest
HP:0032906Focal head nodding automatism seizure
HP:0045084Limb myoclonus
Очень редкий (1–4%)3
HP:0002133Status epilepticus
HP:0011171Simple febrile seizures
HP:0011182Interictal epileptiform activity
Исключён (0%)2
HP:0002361Psychomotor deterioration
HP:0410263Brain imaging abnormality

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы