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Renal agenesis, unilateral

ORPHA:93100Clinical subtypeAutosomal dominantAll ages, Antenatal

Ассоциированные гены (8)

RET
ret proto-oncogene
Disease-causing germline mutation(s) in
OMIM: 164761
FRAS1
Fraser extracellular matrix complex subunit 1
Disease-causing germline mutation(s) in
OMIM: 607830
BMP4
bone morphogenetic protein 4
Disease-causing germline mutation(s) in
OMIM: 112262
FREM2
FRAS1 related extracellular matrix 2
Disease-causing germline mutation(s) in
OMIM: 608945
FREM1
FRAS1 related extracellular matrix 1
Disease-causing germline mutation(s) in
OMIM: 608944
UPK3A
uroplakin 3A
Disease-causing germline mutation(s) in
OMIM: 611559
DSTYK
dual serine/threonine and tyrosine protein kinase
Disease-causing germline mutation(s) in
OMIM: 612666
GREB1L
GREB1 like retinoic acid receptor coactivator
Disease-causing germline mutation(s) (loss of function) in
OMIM: 617782

Эпидемиология (2)

Point prevalence
Unknown
Europe
Prevalence at birth
1-5 / 10 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы