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Thyroid ectopia

ORPHA:95712Morphological anomalyNot applicableInfancy, Neonatal

Ассоциированные гены (2)

NKX2-5
NK2 homeobox 5
Disease-causing germline mutation(s) in
OMIM: 600584
PAX8
paired box 8
Disease-causing germline mutation(s) (loss of function) in
OMIM: 167415

Фенотипы (26)

Облигатный (100%)1
HP:0100028Ectopic thyroid
Очень частый (80–99%)15
HP:0000158Macroglossia
HP:0000239Large fontanelles
HP:0000271Abnormality of the face
HP:0000280Coarse facial features
HP:0000820Abnormality of the thyroid gland
HP:0000821Hypothyroidism
HP:0000952Jaundice
HP:0001252Hypotonia
HP:0001324Muscle weakness
HP:0001537Umbilical hernia
HP:0002019Constipation
HP:0002925Elevated circulating thyroid-stimulating hormone concentration
HP:0003270Abdominal distention
HP:0100029Lingual thyroid
HP:0100786Hypersomnia
Частый (30–79%)8
HP:0010864Intellectual disability, severe
HP:0012378Fatigue
HP:6000855Cold intolerance
HP:0000958Dry skin
HP:0001263Global developmental delay
HP:0001510Growth delay
HP:0001609Hoarse voice
HP:0004322Short stature
Периодический (5–29%)2
HP:0001618Dysphonia
HP:0002015Dysphagia

Эпидемиология (1)

Point prevalence
1-5 / 10 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы