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Cushing disease

ORPHA:96253DiseaseNot applicableAdult

Ассоциированные гены (7)

CDH23
cadherin related 23
Major susceptibility factor in
OMIM: 605516
USP48
ubiquitin specific peptidase 48
Disease-causing somatic mutation(s) in
OMIM: 617445
BRAF
B-Raf proto-oncogene, serine/threonine kinase
Disease-causing somatic mutation(s) in
OMIM: 164757
USP8
ubiquitin specific peptidase 8
Disease-causing somatic mutation(s) in
OMIM: 603158
NR3C1
nuclear receptor subfamily 3 group C member 1
Disease-causing somatic mutation(s) in
OMIM: 138040
TP53
tumor protein p53
Disease-causing somatic mutation(s) in
OMIM: 191170
ATRX
ATRX chromatin remodeler
Disease-causing somatic mutation(s) in
OMIM: 300032

Фенотипы (64)

Очень частый (80–99%)4
HP:0003118Increased circulating cortisol level
HP:0003466Paradoxical increased cortisol secretion on dexamethasone suppression test
HP:0008291Pituitary corticotropic cell adenoma
HP:0012030Increased urinary cortisol level
Частый (30–79%)32
HP:0000939Osteoporosis
HP:0000953Hyperpigmentation of the skin
HP:0000963Thin skin
HP:0000978Bruising susceptibility
HP:0001007Hirsutism
HP:0001050Plethora
HP:0001058Poor wound healing
HP:0001061Acne
HP:0001065Striae distensae
HP:0001324Muscle weakness
HP:0001626Abnormality of the cardiovascular system
HP:0001888Lymphopenia
HP:0001956Truncal obesity
HP:0001974Leukocytosis
HP:0002721Immunodeficiency
HP:0003154Increased circulating ACTH level
HP:0004324Increased body weight
HP:0007126Proximal amyotrophy
HP:0008221Adrenal hyperplasia
HP:0010284Intra-oral hyperpigmentation
HP:0012743Abdominal obesity
HP:0025017Capillary fragility
HP:0025383Dorsocervical fat pad
HP:0000141Amenorrhea
HP:0000708Atypical behavior
HP:0000712Emotional lability
HP:0000819Diabetes mellitus
HP:0000822Hypertension
HP:0031891Decreased eosinophil count
HP:0040270Impaired glucose tolerance
HP:0500011Moon facies
HP:0030200Fatiguable weakness of proximal limb muscles
Периодический (5–29%)20
HP:0000716Depression
HP:0000725Psychotic episodes
HP:0000869Secondary amenorrhea
HP:0000876Oligomenorrhea
HP:0000979Purpura
HP:0001297Stroke
HP:0001658Myocardial infarction
HP:0002086Abnormality of the respiratory system
HP:0002209Sparse scalp hair
HP:0002315Headache
HP:0002354Memory impairment
HP:0002690Large sella turcica
HP:0002953Vertebral compression fracture
HP:0011370Recurrent cutaneous fungal infections
HP:0031284Flushing
HP:0031364Ecchymosis
HP:0031589Suicidal ideation
HP:0031845Abnormal libido
HP:0033505Livedo reticularis
HP:0200042Skin ulcer
Очень редкий (1–4%)8
HP:0000709Psychosis
HP:0000726Dementia
HP:0001123Visual field defect
HP:0007807Optic nerve compression
HP:0010741Pedal edema
HP:0010885Avascular necrosis
HP:0011999Paranoia
HP:0025269Panic attack

Эпидемиология (2)

Point prevalence
1-9 / 100 000
Europe
Annual incidence
1-9 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы