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Posterior polymorphous corneal dystrophy

ORPHA:98973DiseaseAutosomal dominantChildhood

Ассоциированные гены (5)

VSX1
visual system homeobox 1
Disease-causing germline mutation(s) in
OMIM: 605020
ZEB1
zinc finger E-box binding homeobox 1
Disease-causing germline mutation(s) in
OMIM: 189909
COL8A2
collagen type VIII alpha 2 chain
Disease-causing germline mutation(s) in
OMIM: 120252
OVOL2
ovo like zinc finger 2
Disease-causing germline mutation(s) in
OMIM: 616441
GRHL2
grainyhead like transcription factor 2
Disease-causing germline mutation(s) in
OMIM: 608576

Фенотипы (20)

Очень частый (80–99%)2
HP:0011490Abnormal Descemet membrane morphology
HP:0011491Reduced number of corneal endothelial cells
Периодический (5–29%)8
HP:0000483Astigmatism
HP:0000646Amblyopia
HP:0007663Reduced visual acuity
HP:0011483Anterior synechiae of the anterior chamber
HP:0012040Corneal stromal edema
HP:0025358Uveal ectropion
HP:0032122Very low visual acuity
HP:0100692Increased corneal curvature
Очень редкий (1–4%)10
HP:0000501Glaucoma
HP:0000565Esotropia
HP:0000613Photophobia
HP:0000622Blurred vision
HP:0000632Lacrimation abnormality
HP:0007906Ocular hypertension
HP:0007957Corneal opacity
HP:0009918Ectopia pupillae
HP:0200026Ocular pain
HP:0200065Chorioretinal degeneration

Эпидемиология (2)

Point prevalence
1-9 / 100 000
Czech Republic
Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы