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Embryonal rhabdomyosarcoma

ORPHA:99757Clinical subtypeMultigenic/multifactorial

Ассоциированные гены (4)

SLC67A1
solute carrier family 67 member 1
Candidate gene tested in
OMIM: 602631
TP53
tumor protein p53
Disease-causing germline mutation(s) in
OMIM: 191170
NF1
neurofibromin 1
Disease-causing somatic mutation(s) in
OMIM: 613113
DICER1
dicer 1, ribonuclease III
Disease-causing somatic mutation(s) in
OMIM: 606241

Эпидемиология (23)

Annual incidence
<1 / 1 000 000
Austria
Annual incidence
<1 / 1 000 000
Belgium
Annual incidence
<1 / 1 000 000
Bulgaria
Annual incidence
<1 / 1 000 000
Croatia
Annual incidence
<1 / 1 000 000
Czech Republic
Annual incidence
<1 / 1 000 000
Estonia
Annual incidence
<1 / 1 000 000
Finland
Annual incidence
<1 / 1 000 000
Germany
Annual incidence
<1 / 1 000 000
Ireland
Annual incidence
<1 / 1 000 000
Italy
Annual incidence
<1 / 1 000 000
Latvia
Annual incidence
<1 / 1 000 000
Lithuania
Annual incidence
<1 / 1 000 000
Norway
Annual incidence
<1 / 1 000 000
Poland
Annual incidence
<1 / 1 000 000
Portugal
Annual incidence
<1 / 1 000 000
Slovakia
Annual incidence
<1 / 1 000 000
Slovenia
Annual incidence
<1 / 1 000 000
Spain
Annual incidence
<1 / 1 000 000
Switzerland
Annual incidence
<1 / 1 000 000
Netherlands
Annual incidence
<1 / 1 000 000
United Kingdom
Annual incidence
1-9 / 1 000 000
Iceland
Annual incidence
1-9 / 1 000 000
Malta

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы