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Semantic dementia

ORPHA:100069DiseaseMultigenic/multifactorial, Not applicableAdult

Ассоциированные гены (7)

PSEN1
presenilin 1
Disease-causing germline mutation(s) in
OMIM: 104311
TMEM106B
transmembrane protein 106B
Major susceptibility factor in
OMIM: 613413
CHMP2B
charged multivesicular body protein 2B
Major susceptibility factor in
OMIM: 609512
TREM2
triggering receptor expressed on myeloid cells 2
Major susceptibility factor in
OMIM: 605086
MAPT
microtubule associated protein tau
Major susceptibility factor in
OMIM: 157140
GRN
granulin precursor
Major susceptibility factor in
OMIM: 138945
C9ORF72
C9orf72-SMCR8 complex subunit
Major susceptibility factor in
OMIM: 614260

Фенотипы (10)

Очень частый (80–99%)4
HP:0002381Aphasia
HP:0012444Brain atrophy
HP:0030222Visual agnosia
HP:0030784Anomia
Частый (30–79%)6
HP:0000726Dementia
HP:0002167Abnormality of speech or vocalization
HP:0010522Dyslexia
HP:0010523Alexia
HP:0010526Dysgraphia
HP:0012671Abulia

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы