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Osteogenesis imperfecta type 2

ORPHA:216804Clinical subtypeAutosomal dominant, Autosomal recessiveAntenatal, Neonatal

Ассоциированные гены (6)

COL1A1
collagen type I alpha 1 chain
Disease-causing germline mutation(s) in
OMIM: 120150
COL1A2
collagen type I alpha 2 chain
Disease-causing germline mutation(s) in
OMIM: 120160
P3H1
prolyl 3-hydroxylase 1
Disease-causing germline mutation(s) in
OMIM: 610339
CRTAP
cartilage associated protein
Disease-causing germline mutation(s) in
OMIM: 605497
PPIB
peptidylprolyl isomerase B
Disease-causing germline mutation(s) in
OMIM: 123841
MESD
mesoderm development LRP chaperone
Disease-causing germline mutation(s) (loss of function) in
OMIM: 607783

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы