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Total early-onset cataract

ORPHA:98994Clinical subtypeAutosomal dominant, Autosomal recessiveInfancy, Neonatal

Ассоциированные гены (17)

CRYAA
crystallin alpha A
Disease-causing germline mutation(s) in
OMIM: 123580
CRYBB2
crystallin beta B2
Disease-causing germline mutation(s) in
OMIM: 123620
GJA8
gap junction protein alpha 8
Disease-causing germline mutation(s) in
OMIM: 600897
HSF4
heat shock transcription factor 4
Disease-causing germline mutation(s) in
OMIM: 602438
MIP
major intrinsic protein of lens fiber
Disease-causing germline mutation(s) in
OMIM: 154050
NHS
NHS actin remodeling regulator
Candidate gene tested in
OMIM: 300457
LIM2
lens intrinsic membrane protein 2
Disease-causing germline mutation(s) in
OMIM: 154045
EPHA2
EPH receptor A2
Disease-causing germline mutation(s) in
OMIM: 176946
FYCO1
FYVE and coiled-coil domain autophagy adaptor 1
Disease-causing germline mutation(s) in
OMIM: 607182
AGK
acylglycerol kinase
Disease-causing germline mutation(s) in
OMIM: 610345
CRYGB
crystallin gamma B
Disease-causing germline mutation(s) in
OMIM: 123670
GCNT2
glucosaminyl (N-acetyl) transferase 2 (I blood group)
Disease-causing germline mutation(s) in
OMIM: 600429
LSS
lanosterol synthase
Disease-causing germline mutation(s) in
OMIM: 600909
PGRMC1
progesterone receptor membrane component 1
Disease-causing germline mutation(s) in
OMIM: 300435
LEMD2
LEM domain nuclear envelope protein 2
Disease-causing germline mutation(s) in
OMIM: 616312
DNMBP
dynamin binding protein
Disease-causing germline mutation(s) (loss of function) in
OMIM: 611282
SIPA1L3
signal induced proliferation associated 1 like 3
Disease-causing germline mutation(s) in
OMIM: 616655

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы