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Autosomal recessive non-syndromic intellectual disability

ORPHA:88616Etiological subtypeAutosomal recessiveChildhood, Infancy

Ассоциированные гены (54)

DCPS
decapping enzyme, scavenger
Disease-causing germline mutation(s) in
OMIM: 610534
B3GALNT2
beta-1,3-N-acetylgalactosaminyltransferase 2
Disease-causing germline mutation(s) in
OMIM: 610194
IMPA1
inositol monophosphatase 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 602064
ABCA2
ATP binding cassette subfamily A member 2
Disease-causing germline mutation(s) in
OMIM: 600047
CHKA
choline kinase alpha
Disease-causing germline mutation(s) in
OMIM: 118491
GRIA1
glutamate ionotropic receptor AMPA type subunit 1
Disease-causing germline mutation(s) in
OMIM: 138248
CEP104
centrosomal protein 104
Disease-causing germline mutation(s) in
OMIM: 616690
GRIN1
glutamate ionotropic receptor NMDA type subunit 1
Disease-causing germline mutation(s) in
OMIM: 138249
AIMP1
aminoacyl tRNA synthetase complex interacting multifunctional protein 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 603605
CRBN
cereblon
Disease-causing germline mutation(s) in
OMIM: 609262
TUSC3
tumor suppressor candidate 3
Disease-causing germline mutation(s) in
OMIM: 601385
TECR
trans-2,3-enoyl-CoA reductase
Disease-causing germline mutation(s) in
OMIM: 610057
GRIK2
glutamate ionotropic receptor kainate type subunit 2
Disease-causing germline mutation(s) (loss of function) in
OMIM: 138244
WASHC4
WASH complex subunit 4
Disease-causing germline mutation(s) in
OMIM: 615748
TRAPPC9
trafficking protein particle complex subunit 9
Disease-causing germline mutation(s) (loss of function) in
OMIM: 611966
PRSS12
serine protease 12
Disease-causing germline mutation(s) in
OMIM: 606709
MED23
mediator complex subunit 23
Disease-causing germline mutation(s) in
OMIM: 605042
CRADD
CARD and death domain containing adaptor protein
Disease-causing germline mutation(s) in
OMIM: 603454
ZC3H14
zinc finger CCCH-type containing 14
Disease-causing germline mutation(s) in
OMIM: 613279
NSUN2
NOP2/Sun RNA methyltransferase 2
Disease-causing germline mutation(s) in
OMIM: 610916
LINS1
lines homolog 1
Disease-causing germline mutation(s) in
OMIM: 610350
PGAP1
post-GPI attachment to proteins inositol deacylase 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 611655
METTL23
methyltransferase 23, arginine
Disease-causing germline mutation(s) in
OMIM: 615262
CLIP1
CAP-Gly domain containing linker protein 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 179838
FBXO31
F-box protein 31
Disease-causing germline mutation(s) (loss of function) in
OMIM: 609102
NDST1
N-deacetylase and N-sulfotransferase 1
Disease-causing germline mutation(s) in
OMIM: 600853
FMN2
formin 2
Disease-causing germline mutation(s) in
OMIM: 606373
EDC3
enhancer of mRNA decapping 3
Disease-causing germline mutation(s) in
OMIM: 609842
HNMT
histamine N-methyltransferase
Disease-causing germline mutation(s) in
OMIM: 605238
EZR
ezrin
Disease-causing germline mutation(s) (loss of function) in
OMIM: 123900
LMAN2L
lectin, mannose binding 2 like
Disease-causing germline mutation(s) in
OMIM: 609552
NEMF
nuclear export mediator factor
Disease-causing germline mutation(s) in
OMIM: 608378
GRM7
glutamate metabotropic receptor 7
Disease-causing germline mutation(s) in
OMIM: 604101
IQSEC1
IQ motif and Sec7 domain ArfGEF 1
Disease-causing germline mutation(s) in
OMIM: 610166
TNIK
TRAF2 and NCK interacting kinase
Disease-causing germline mutation(s) (loss of function) in
OMIM: 610005
NCDN
neurochondrin
Disease-causing germline mutation(s) in
OMIM: 608458
UBE4A
ubiquitination factor E4A
Disease-causing germline mutation(s) (loss of function) in
OMIM: 603753
TTC5
tetratricopeptide repeat domain 5
Disease-causing germline mutation(s) (loss of function) in
OMIM: 619014
PIGC
phosphatidylinositol glycan anchor biosynthesis class C
Disease-causing germline mutation(s) in
OMIM: 601730
SLC45A1
solute carrier family 45 member 1
Disease-causing germline mutation(s) in
OMIM: 605763
GEMIN5
gem nuclear organelle associated protein 5
Disease-causing germline mutation(s) (loss of function) in
OMIM: 607005
FRRS1L
ferric chelate reductase 1 like
Disease-causing germline mutation(s) in
OMIM: 604574
ALKBH8
alkB homolog 8, tRNA methyltransferase
Disease-causing germline mutation(s) (loss of function) in
OMIM: 613306
MBOAT7
membrane bound acylglycerophosphatidylinositol O-acyltransferase MBOAT7
Disease-causing germline mutation(s) (loss of function) in
OMIM: 606048
FERRY3
FERRY endosomal RAB5 effector complex subunit 3
Disease-causing germline mutation(s) in
OMIM: 616082
SARS1
seryl-tRNA synthetase 1
Disease-causing germline mutation(s) in
OMIM: 607529
RSRC1
arginine and serine rich coiled-coil 1
Disease-causing germline mutation(s) in
OMIM: 613352
MED25
mediator complex subunit 25
Disease-causing germline mutation(s) in
OMIM: 610197
NAA20
N-alpha-acetyltransferase 20, NatB catalytic subunit
Disease-causing germline mutation(s) (loss of function) in
OMIM: 610833
CC2D1A
coiled-coil and C2 domain containing 1A
Disease-causing germline mutation(s) in
OMIM: 610055
MAN1B1
mannosidase alpha class 1B member 1
Disease-causing germline mutation(s) in
OMIM: 604346
TPR
translocated promoter region, nuclear basket protein
Disease-causing germline mutation(s) in
OMIM: 189940
KDM5B
lysine demethylase 5B
Disease-causing germline mutation(s) in
OMIM: 605393
EEF1B2
eukaryotic translation elongation factor 1 beta 2
Disease-causing germline mutation(s) in
OMIM: 600655

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы