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Autosomal dominant non-syndromic intellectual disability

ORPHA:178469Etiological subtypeAutosomal dominantChildhood, Infancy

Ассоциированные гены (43)

KCNQ2
potassium voltage-gated channel subfamily Q member 2
Disease-causing germline mutation(s) in
OMIM: 602235
ERBB4
erb-b2 receptor tyrosine kinase 4
Disease-causing germline mutation(s) in
OMIM: 600543
BRSK2
BR serine/threonine kinase 2
Disease-causing germline mutation(s) (loss of function) in
OMIM: 609236
SLC6A1
solute carrier family 6 member 1
Disease-causing germline mutation(s) in
OMIM: 137165
SETD1B
SET domain containing 1B, histone lysine methyltransferase
Disease-causing germline mutation(s) in
OMIM: 611055
CLTC
clathrin heavy chain
Disease-causing germline mutation(s) in
OMIM: 118955
ITSN1
intersectin 1
Disease-causing germline mutation(s) in
OMIM: 602442
PRICKLE2
prickle planar cell polarity protein 2
Disease-causing germline mutation(s) in
OMIM: 608501
HIVEP2
HIVEP zinc finger 2
Disease-causing germline mutation(s) (loss of function) in
OMIM: 143054
KDM5B
lysine demethylase 5B
Candidate gene tested in
OMIM: 605393
GABBR1
gamma-aminobutyric acid type B receptor subunit 1
Disease-causing germline mutation(s) in
OMIM: 603540
DPYSL2
dihydropyrimidinase like 2
Disease-causing germline mutation(s) in
OMIM: 602463
SET
SET nuclear proto-oncogene
Disease-causing germline mutation(s) in
OMIM: 600960
ARF3
ARF GTPase 3
Disease-causing germline mutation(s) in
OMIM: 103190
CACNA1I
calcium voltage-gated channel subunit alpha1 I
Disease-causing germline mutation(s) in
OMIM: 608230
RAB11A
RAB11A, member RAS oncogene family
Disease-causing germline mutation(s) in
OMIM: 605570
PPP3CA
protein phosphatase 3 catalytic subunit alpha
Disease-causing germline mutation(s) in
OMIM: 114105
GRIA1
glutamate ionotropic receptor AMPA type subunit 1
Disease-causing germline mutation(s) in
OMIM: 138248
KCNQ5
potassium voltage-gated channel subfamily Q member 5
Disease-causing germline mutation(s) in
OMIM: 607357
DLL1
delta like canonical Notch ligand 1
Disease-causing germline mutation(s) in
OMIM: 606582
SCN8A
sodium voltage-gated channel alpha subunit 8
Disease-causing germline mutation(s) in
OMIM: 600702
TAOK1
TAO kinase 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 610266
TRPM3
transient receptor potential cation channel subfamily M member 3
Disease-causing germline mutation(s) in
OMIM: 608961
NBEA
neurobeachin
Disease-causing germline mutation(s) in
OMIM: 604889
CIC
capicua transcriptional repressor
Disease-causing germline mutation(s) (loss of function) in
OMIM: 612082
CSNK2B
casein kinase 2 beta
Disease-causing germline mutation(s) (loss of function) in
OMIM: 115441
ASH1L
ASH1 like histone lysine methyltransferase
Disease-causing germline mutation(s) in
OMIM: 607999
SEMA6B
semaphorin 6B
Disease-causing germline mutation(s) in
OMIM: 608873
CUX1
cut like homeobox 1
Disease-causing germline mutation(s) in
OMIM: 116896
YWHAZ
tyrosine 3-monooxygenase/tryptophan 5-monooxygenase activation protein zeta
Disease-causing germline mutation(s) in
OMIM: 601288
TCF4
transcription factor 4
Disease-causing germline mutation(s) in
OMIM: 602272
CTNND2
catenin delta 2
Disease-causing germline mutation(s) in
OMIM: 604275
KIRREL3
kirre like nephrin family adhesion molecule 3
Disease-causing germline mutation(s) in
OMIM: 607761
DOCK8
dedicator of cytokinesis 8
Disease-causing germline mutation(s) in
OMIM: 611432
MBD5
methyl-CpG binding domain protein 5
Disease-causing germline mutation(s) in
OMIM: 611472
CDH15
cadherin 15
Disease-causing germline mutation(s) in
OMIM: 114019
GRIN1
glutamate ionotropic receptor NMDA type subunit 1
Disease-causing germline mutation(s) in
OMIM: 138249
DYNC1H1
dynein cytoplasmic 1 heavy chain 1
Disease-causing germline mutation(s) in
OMIM: 600112
CACNG2
calcium voltage-gated channel auxiliary subunit gamma 2
Disease-causing germline mutation(s) in
OMIM: 602911
EPB41L1
erythrocyte membrane protein band 4.1 like 1
Disease-causing germline mutation(s) in
OMIM: 602879
EEF1A2
eukaryotic translation elongation factor 1 alpha 2
Disease-causing germline mutation(s) in
OMIM: 602959
CAMK2A
calcium/calmodulin dependent protein kinase II alpha
Disease-causing germline mutation(s) in
OMIM: 114078
CAMK2B
calcium/calmodulin dependent protein kinase II beta
Disease-causing germline mutation(s) in
OMIM: 607707

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы