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Rare autosomal recessive non-syndromic sensorineural deafness type DFNB

ORPHA:90636Etiological subtypeAutosomal recessiveInfancy, Neonatal

Ассоциированные гены (74)

PPIP5K2
diphosphoinositol pentakisphosphate kinase 2
Disease-causing germline mutation(s) in
OMIM: 611648
TMEM132E
transmembrane protein 132E
Disease-causing germline mutation(s) in
OMIM: 616178
GRAP
GRB2 related adaptor protein
Disease-causing germline mutation(s) in
OMIM: 604330
BDP1
BDP1 general transcription factor IIIB subunit
Disease-causing germline mutation(s) in
OMIM: 607012
AFG2B
AAA ATPase AFG2B
Disease-causing germline mutation(s) in
OMIM: 619578
CEACAM16
CEA cell adhesion molecule 16, tectorial membrane component
Disease-causing germline mutation(s) in
OMIM: 614591
NARS2
asparaginyl-tRNA synthetase 2, mitochondrial
Disease-causing germline mutation(s) in
OMIM: 612803
ROR1
receptor tyrosine kinase like orphan receptor 1
Disease-causing germline mutation(s) in
OMIM: 602336
WBP2
WW domain binding protein 2
Disease-causing germline mutation(s) in
OMIM: 606962
EPS8L2
EPS8 signaling adaptor L2
Disease-causing germline mutation(s) in
OMIM: 614988
SLC26A4
solute carrier family 26 member 4
Disease-causing germline mutation(s) in
OMIM: 605646
BSND
barttin CLCNK type accessory subunit beta
Disease-causing germline mutation(s) in
OMIM: 606412
CDH23
cadherin related 23
Disease-causing germline mutation(s) in
OMIM: 605516
TECTA
tectorin alpha
Disease-causing germline mutation(s) in
OMIM: 602574
TMC1
transmembrane channel like 1
Disease-causing germline mutation(s) in
OMIM: 606706
TMIE
transmembrane inner ear
Disease-causing germline mutation(s) in
OMIM: 607237
TMPRSS3
transmembrane serine protease 3
Disease-causing germline mutation(s) in
OMIM: 605511
USH1C
USH1 protein network component harmonin
Disease-causing germline mutation(s) in
OMIM: 605242
COL11A2
collagen type XI alpha 2 chain
Disease-causing germline mutation(s) in
OMIM: 120290
ELMOD3
ELMO domain containing 3
Disease-causing germline mutation(s) in
OMIM: 615427
GJB2
gap junction protein beta 2
Disease-causing germline mutation(s) in
OMIM: 121011
GJB3
gap junction protein beta 3
Disease-causing germline mutation(s) in
OMIM: 603324
GJB6
gap junction protein beta 6
Disease-causing germline mutation(s) in
OMIM: 604418
MET
MET proto-oncogene, receptor tyrosine kinase
Disease-causing germline mutation(s) in
OMIM: 164860
MYO15A
myosin XVA
Disease-causing germline mutation(s) in
OMIM: 602666
MYO6
myosin VI
Disease-causing germline mutation(s) in
OMIM: 600970
MYO7A
myosin VIIA
Disease-causing germline mutation(s) in
OMIM: 276903
OTOF
otoferlin
Disease-causing germline mutation(s) in
OMIM: 603681
PCDH15
protocadherin related 15
Disease-causing germline mutation(s) in
OMIM: 605514
WHRN
whirlin
Disease-causing germline mutation(s) in
OMIM: 607928
STRC
stereocilin
Disease-causing germline mutation(s) in
OMIM: 606440
TRIOBP
TRIO and F-actin binding protein
Disease-causing germline mutation(s) in
OMIM: 609761
RDX
radixin
Disease-causing germline mutation(s) in
OMIM: 179410
LHFPL5
LHFPL tetraspan subfamily member 5
Disease-causing germline mutation(s) in
OMIM: 609427
ESPN
espin
Disease-causing germline mutation(s) in
OMIM: 606351
ESRRB
estrogen related receptor beta
Disease-causing germline mutation(s) in
OMIM: 602167
MARVELD2
MARVEL domain containing 2
Disease-causing germline mutation(s) in
OMIM: 610572
MYO3A
myosin IIIA
Disease-causing germline mutation(s) in
OMIM: 606808
SLC26A5
solute carrier family 26 member 5
Disease-causing germline mutation(s) in
OMIM: 604943
OTOA
otoancorin
Disease-causing germline mutation(s) in
OMIM: 607038
PJVK
pejvakin
Disease-causing germline mutation(s) in
OMIM: 610219
CLDN14
claudin 14
Disease-causing germline mutation(s) in
OMIM: 605608
LRTOMT
leucine rich transmembrane and O-methyltransferase domain containing
Disease-causing germline mutation(s) in
OMIM: 612414
HGF
hepatocyte growth factor
Disease-causing germline mutation(s) in
OMIM: 142409
LOXHD1
lipoxygenase homology PLAT domains 1
Disease-causing germline mutation(s) in
OMIM: 613072
GRXCR1
glutaredoxin and cysteine rich domain containing 1
Disease-causing germline mutation(s) in
OMIM: 613283
TPRN
taperin
Disease-causing germline mutation(s) in
OMIM: 613354
PTPRQ
protein tyrosine phosphatase receptor type Q
Disease-causing germline mutation(s) in
OMIM: 603317
SERPINB6
serpin family B member 6
Disease-causing germline mutation(s) in
OMIM: 173321
TBC1D24
TBC1 domain family member 24
Disease-causing germline mutation(s) in
OMIM: 613577
GPSM2
G protein signaling modulator 2
Disease-causing germline mutation(s) in
OMIM: 609245
MSRB3
methionine sulfoxide reductase B3
Disease-causing germline mutation(s) in
OMIM: 613719
ILDR1
immunoglobulin like domain containing receptor 1
Disease-causing germline mutation(s) in
OMIM: 609739
KARS1
lysyl-tRNA synthetase 1
Disease-causing germline mutation(s) in
OMIM: 601421
GIPC3
GIPC PDZ domain containing family member 3
Disease-causing germline mutation(s) in
OMIM: 608792
CIB2
calcium and integrin binding family member 2
Disease-causing germline mutation(s) in
OMIM: 605564
CABP2
calcium binding protein 2
Disease-causing germline mutation(s) in
OMIM: 607314
OTOG
otogelin
Disease-causing germline mutation(s) in
OMIM: 604487
PNPT1
polyribonucleotide nucleotidyltransferase 1
Disease-causing germline mutation(s) in
OMIM: 610316
OTOGL
otogelin like
Disease-causing germline mutation(s) in
OMIM: 614925
SYNE4
spectrin repeat containing nuclear envelope family member 4
Disease-causing germline mutation(s) in
OMIM: 615535
SLITRK6
SLIT and NTRK like family member 6
Disease-causing germline mutation(s) (loss of function) in
OMIM: 609681
GRXCR2
glutaredoxin and cysteine rich domain containing 2
Disease-causing germline mutation(s) (loss of function) in
OMIM: 615762
EPS8
EGFR pathway substrate 8, signaling adaptor
Disease-causing germline mutation(s) (loss of function) in
OMIM: 600206
ADCY1
adenylate cyclase 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 103072
CLIC5
chloride intracellular channel 5
Disease-causing germline mutation(s) in
OMIM: 607293
RIPOR2
RHO family interacting cell polarization regulator 2
Disease-causing germline mutation(s) in
OMIM: 611410
DCDC2
doublecortin domain containing 2
Disease-causing germline mutation(s) in
OMIM: 605755
ATP2B2
ATPase plasma membrane Ca2+ transporting 2
Modifying germline mutation in
OMIM: 108733
S1PR2
sphingosine-1-phosphate receptor 2
Disease-causing germline mutation(s) (loss of function) in
OMIM: 605111
MPZL2
myelin protein zero like 2
Disease-causing germline mutation(s) in
OMIM: 604873
CDC14A
cell division cycle 14A
Disease-causing germline mutation(s) (loss of function) in
OMIM: 603504
GJA1
gap junction protein alpha 1
Candidate gene tested in
OMIM: 121014
MINAR2
membrane integral NOTCH2 associated receptor 2
Disease-causing germline mutation(s) in
OMIM: 620215

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы